Oncolytic herpes simplex virus expressing yeast cytosine deaminase: relationship between viral replication, transgene expression, prodrug bioactivation

Cancer Gene Ther. 2012 Mar;19(3):160-70. doi: 10.1038/cgt.2011.70. Epub 2011 Nov 11.

Abstract

Yeast cytosine deaminase (yCD) is a well-characterized prodrug/enzyme system that converts 5-fluorocytosine (5-FC) to 5-fluorouracil (5-FU), and has been combined with oncolytic viruses. However, in vivo studies of the interactions between 5-FC bioactivation and viral replication have not been previously reported, nor have the kinetics of transgene expression and the pharmacokinetics of 5-FC and 5-FU. We constructed a replication-conditional Herpes simplex virus 1 (HSV-1) expressing yCD and examined cytotoxicity when 5-FC was initiated at different times after viral infection, and observed that earlier 5-FC administration led to greater cytotoxicity than later 5-FC administration in vitro and in vivo. In animal models, 12 days of 5-FC administration was superior to 6 days, but dosing beyond 12 days did not further enhance efficacy. Consistent with the dosing-schedule results, both viral genomic DNA copy number and viral titers were observed to peak on Day 3 after viral injection and gradually decrease thereafter. The virus is replication-conditional and was detected in tumors for as long as 2 weeks after viral injection. The maximum relative extent of yCD conversion of 5-FC to 5-FU in tumors was observed on Day 6 after viral injection and it decreased progressively thereafter. The observation that 5-FU generation within tumors did not lead to appreciable levels of systemic 5-FU (<10 ng ml⁻¹) is important and has not been previously reported. The approaches used in these studies of the relationship between the viral replication kinetics, transgene expression, prodrug administration and anti-tumor efficacy are useful in the design of clinical trials of armed, oncolytic viruses.

Publication types

  • Research Support, N.I.H., Extramural

MeSH terms

  • Animals
  • Antimetabolites, Antineoplastic / pharmacokinetics
  • Cell Line, Tumor
  • Chlorocebus aethiops
  • Colonic Neoplasms / genetics
  • Colonic Neoplasms / metabolism
  • Colonic Neoplasms / therapy*
  • Colonic Neoplasms / virology
  • Cytosine Deaminase / biosynthesis*
  • Cytosine Deaminase / genetics
  • Cytosine Deaminase / metabolism
  • Drug Administration Schedule
  • Flucytosine / pharmacokinetics*
  • Fluorouracil / pharmacokinetics*
  • Genetic Therapy / methods
  • Genetic Vectors
  • HT29 Cells
  • Humans
  • Male
  • Mice
  • Mice, Inbred BALB C
  • Oncolytic Virotherapy / methods*
  • Prodrugs / pharmacokinetics*
  • Simplexvirus / enzymology
  • Simplexvirus / genetics
  • Simplexvirus / physiology*
  • Transgenes
  • Virus Replication
  • Xenograft Model Antitumor Assays
  • Yeasts / enzymology
  • Yeasts / genetics

Substances

  • Antimetabolites, Antineoplastic
  • Prodrugs
  • Flucytosine
  • Cytosine Deaminase
  • Fluorouracil