Turbulence Activates Platelet Biogenesis to Enable Clinical Scale Ex Vivo Production

Cell. 2018 Jul 26;174(3):636-648.e18. doi: 10.1016/j.cell.2018.06.011. Epub 2018 Jul 12.

Abstract

The ex vivo generation of platelets from human-induced pluripotent cells (hiPSCs) is expected to compensate donor-dependent transfusion systems. However, manufacturing the clinically required number of platelets remains unachieved due to the low platelet release from hiPSC-derived megakaryocytes (hiPSC-MKs). Here, we report turbulence as a physical regulator in thrombopoiesis in vivo and its application to turbulence-controllable bioreactors. The identification of turbulent energy as a determinant parameter allowed scale-up to 8 L for the generation of 100 billion-order platelets from hiPSC-MKs, which satisfies clinical requirements. Turbulent flow promoted the release from megakaryocytes of IGFBP2, MIF, and Nardilysin to facilitate platelet shedding. hiPSC-platelets showed properties of bona fide human platelets, including circulation and hemostasis capacities upon transfusion in two animal models. This study provides a concept in which a coordinated physico-chemical mechanism promotes platelet biogenesis and an innovative strategy for ex vivo platelet manufacturing.

Keywords: IGFBP2; MIF; Nardilysin; bioreactor; iPSC; megakaryocyte; platelet; regenerative medicine; shear stress; turbulence.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Bioreactors
  • Blood Platelets / metabolism*
  • Cell Culture Techniques / instrumentation
  • Cell Culture Techniques / methods*
  • Humans
  • Hydrodynamics
  • Induced Pluripotent Stem Cells / metabolism
  • Megakaryocytes / metabolism
  • Megakaryocytes / physiology
  • Thrombopoiesis / physiology*