Predicate |
Object |
assignee |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentassignee/MD5_a6748c1fba1292abba86450fa886727c |
classificationCPCAdditional |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61K48-0083 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61K48-0058 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2750-14141 |
classificationCPCInventive |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C07K14-4716 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61K48-005 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61K48-0058 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61K48-0075 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N15-86 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61P21-00 |
classificationIPCInventive |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/A61K48-00 http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/C12N15-86 |
filingDate |
2019-06-17^^<http://www.w3.org/2001/XMLSchema#date> |
inventor |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_b2761ec2c1bacb3e67b536bc1ee711a7 http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_dba6fe32ed46ec4283a0bd81cfe2d700 |
publicationDate |
2019-12-26^^<http://www.w3.org/2001/XMLSchema#date> |
publicationNumber |
WO-2019245973-A1 |
titleOfInvention |
Adeno-associated virus vector delivery of muscle specific micro-dystrophin to treat muscular dystrophy |
abstract |
The invention provides gene therapy vectors, such as adeno-associated virus (AAV) vectors, expressing a miniaturized human micro-dystrophin gene and method of using these vectors to express micro-dystrophin in skeletal muscle s including diaphragm and cardiac muscle and to protect muscle fibers from injury, increase muscle strength and reduce and/or prevent fibrosis in subjects suffering from muscular dystrophy. |
isCitedBy |
http://rdf.ncbi.nlm.nih.gov/pubchem/patent/WO-2022091025-A1 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11406717-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11723986-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11298429-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/WO-2021257595-A1 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/WO-2021138286-A1 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11534501-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/WO-2022245675-A1 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11535868-B2 |
priorityDate |
2018-06-18^^<http://www.w3.org/2001/XMLSchema#date> |
type |
http://data.epo.org/linked-data/def/patent/Publication |