Predicate |
Object |
assignee |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentassignee/MD5_a6748c1fba1292abba86450fa886727c http://rdf.ncbi.nlm.nih.gov/pubchem/patentassignee/MD5_f55eb3b66100f6d553bdcf54765c9392 |
classificationCPCAdditional |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2750-14171 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2750-14143 |
classificationCPCInventive |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N15-86 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61K48-005 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61K48-0075 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C07K14-705 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C07K14-47 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61P27-02 |
classificationIPCInventive |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/A61K48-00 http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/C07K14-47 |
filingDate |
2020-04-15^^<http://www.w3.org/2001/XMLSchema#date> |
inventor |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_95c7cf80d019562dfd202d1de32e9dfb http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_e7d8391f8329d51abe3e7ad0a9f8bff4 http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_8cd3fd45d6a653f0eb63d907430c6a7c http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_d54299022084ee6dc3b40867bdf348ba |
publicationDate |
2020-10-22^^<http://www.w3.org/2001/XMLSchema#date> |
publicationNumber |
WO-2020214737-A1 |
titleOfInvention |
Gene therapy for treating or preventing visual effects in batten disease |
abstract |
The present disclosure relates to gene therapy methods of preserving photoreceptors and/or inhibiting or preventing retinal degeneration in Batten disease patients, including recombinant adeno-associated virus (rAAV) delivery of a neuronal ceroid lipofuscinosis neuronal 6 (CLN6) polynucleotide. |
priorityDate |
2019-04-15^^<http://www.w3.org/2001/XMLSchema#date> |
type |
http://data.epo.org/linked-data/def/patent/Publication |